
On 28th February 2022, Health and Social Care Secretary Sajid Javid launched England’s first Rare...
Read moreInnovative therapies for rare diseases may only be available in a select number of countries in Euro...
Read moreNICE’s Highly-Specialised Technologies (HST) process is a method for evaluating medicines and trea...
Read moreThis article discusses updates to the orphan drugs and diseases landscapes, the challenges and incen...
Read moreFaster access to new treatments for very rare conditions announced following a revised decision maki...
Read moreNew doctrine accelerates drug development for rare diseases and oncology by adjusting evidence requi...
Read moreThis reforms have been welcomed by the industry as they should support faster access to medicines as...
Read moreWith many anticipated new medicines for rare diseases, countries are beginning to prepare appropriat...
Read moreThis study investigates costs of gene/acute therapies versus chronic treatments for rare diseases, o...
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