Search results for: rare disease

PMA Insights: Week 14

We summarise key pharmaceutical, pricing and market access insights that are worth reading about thi...

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IPCEI to promote development of gene and cell ther

The IPCEI was signed to address the need to equip Europe with a strong, innovative and export-friend...

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UK-wide commitments for genomics initiatives

According to the Department of Health and Social Care (DHSC), the commitments will enable patients t...

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Orphan status higher prices in the UK

Beyond the regulatory level, a well-recognised challenge for companies launching drugs in orphan dis...

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Ensuring patients have access to orphan drugs

According to the pharmaceutical industry association, Farmaindustria, 40% of orphan drugs approved i...

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China's most recent NRDL update

In December 2021, China once again updated its National Reimbursed Drugs List (NRDL).

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Institute of Cancer Research labels NICE

In a statement the ICR said that it welcomes some of the changes, but that it wants to “see furthe...

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NHS England announces access deal for Libmeldy

The news comes after the health service negotiated a “significant confidential discount” to the ...

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Developing a STA/HST submission to NICE

NICE require a broad range of evidence to be included within the reimbursement dossier, including cl...

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NICE changes to its methods and processes

The changes cover how topics are chosen, the steps and stages in each evaluation and how evidence is...

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